Dr. Paola Leone

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Dr. Paola Leone’s recent work focuses on the development of a novel gene therapy technology selectively developed to target and repair white matter and prevent disease progression in Canavan Disease. This could also benefit other leukodystrophies.  She is a subject of the documentary film, “Little Heroes”, a documentary inspired by the experiences of seven children and their families confronted with a diagnosis of Canavan disease. Check out Little Heroes on Amazon – free with Prime!! […]